Select Country

877-783-6728 (877-StemSave)

StemSave Blog

Stem Cell Clinical Trials to Treat Genetic Disorders Announced

Posted by on Aug 1, 2013 8:03:20 AM

DNA strand

Gene therapies utilizing stem cells are being developed that may lead to a cure for several genetic diseases. Currently, two clinical trials were announced to treat Cerebral Adrenoleukodystrophy (CCALD) and beta-thalassemia/sickle cell disease.

This type of gene therapy is often referred to as translational genomics. The clinical trials involve extracting the stem cells from the patient, replacing the defective gene with the corrective gene in vitro [outside the body] and transplanting the stem cells back into the patient, where they continue to multiply and replace the cells with the defective gene.

The success of these trials – being conducted by BlueBird Bio, Inc. provides a blueprint for therapies to treat a broad range of genetic disease. For individuals or families with a history of genetic disorders, the wisdom of banking your own valuable stem cells when they are young, vital and plentiful is therefore apparent. The most convenient and affordable method of securing the unique properties of stem cells is through the dental pulp in teeth, which are readily extracted or are naturally shed during childhood and young adult years.

To learn more about stem cells, and how families can now easily preserve their own dental stem cells for use in future therapies, visit StemSave or call 877-783-6728 (877-StemSave) today.

To view the beta-thalassemia/sickle cell disease clinical trial, click here.

To view the Cerebral Adrenoleukodystrophy (CCALD) clinical trial, click here.

The future of Regenerative Medicine is now.™

Topics: sickle cell disease, Phase III, stemsaveblog, Cerebral Adrenoleukodystrophy, clinical trials, Beta-thalassemia, Stemcells, translational genomics, autologousstemcells, young stem cells


AAOMS - American Association of Oral and Maxillofacial Surgeons


As the industry leader, StemSave is the only stem cell banking service to be designated as an ASI approved program.

    Recent Posts

    Posts by Topic

    see all